Gene therapy 1

Gene therapy is introduction of normal genes in place of missing or defective gene to correct a genetic disorder. 

Types.

Method

First therapy in 1990 for immunodeficiency disease. Can treat adenosine deaminase deficiency ADA,  Thalassemia and hunters disease. 

2019 crisper based gene editing in human editing gene therapy will be conducted. To treat leber congenital amaurosis. 

Advantages. 
Risks